GovernmentUnited Kingdom Official institution
UK clears triheptanoin, sold as Dojolvi, for rare inherited disorders in adults and children
The UK medicines regulator, the MHRA, has cleared triheptanoin, sold as Dojolvi, to treat adult and paediatric patients with a group of rare inherited disorders.
This summary was generated by AI; the official source prevails.
What does it mean?
A medicine called triheptanoin, sold as Dojolvi, can now be used in the UK to treat rare inherited conditions in both adults and children.
Who is affected?
Adults and children in the UK with a group of rare inherited disorders.